Search for Clinical Trial Results
Niemann-Pick Diseases - 25 Studies Found
Status | Study |
Recruiting |
Study Name: A Long-Term Study of Olipudase Alfa in Patients With Acid Sphingomyelinase Deficiency Condition: Sphingomyelin Lipidosis Date: 2013-11-26 Interventions: Drug: GZ402665 Pharmaceutical form: Powder for concentrate |
Completed |
Study Name: Saccadic Eye Movements in Patients With Niemann-Pick Type C Disease Condition: Niemann Pick Diseases Date: 2006-04-19 Interventions: Drug: OGT918 |
Recruiting |
Study Name: Efficacy, Safety, Pharmacodynamic, and Pharmacokinetics Study of Olipudase Alfa in Patients With Acid Sphingomyelinase Deficiency Condition: Sphingomyelin Lipidosis Date: 2013-11-26 Interventions:
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Recruiting |
Study Name: Safety, Tolerability, PK, and Efficacy Evaluation of Repeat Ascending Doses of Olipudase Alfa in Pediatric Patients <18 Years of Age With Acid Sphingomyelinase Deficiency Condition: Sphingomyelin Lipidosis Date: 2014-11-07 Interventions: Drug: Olipudase alfa Pharmaceutical form: powder for concentrate for solution for infusion Route of admi |
Recruiting |
Study Name: Study of the Pharmacokinetics of Trappsol and Effects on Potential Biomarkers of Niemann-Pick C1 (NPC1) Condition: Niemann-Pick Disease, Type C1 Date: 2016-09-21 Interventions: Drug: Hydroxypropyl-beta-cyclodextrin Used in the treatment of Niemann-Pick Disease C1 ( NPC1) |
Recruiting |
Study Name: Study of Pharmacokinetics and Preliminary Efficacy in Patients With Niemann-Pick C1 Condition: Niemann-Pick Disease, Type C1 Date: 2016-08-19 Interventions: Drug: Hydroxypropyl-beta-cyclodextrin Used in the treatment of Niemann-Pick C1 |
Completed |
Study Name: Application of Miglustat in Patients With Niemann-Pick Type C Condition: Niemann-Pick Disease Type C Date: 2013-01-02 Interventions: Drug: Miglustat miglustat 200mg tid for adult. For children surface area correction will be made. A lowe |
Completed |
Study Name: Hydroxypropyl Beta Cyclodextrin for Niemann-Pick Type C1 Disease Condition: Date: 2024-05-10 |
Terminated |
Study Name: Screening of Niemann-Pick Disease, Type C in a Psychiatric Population Condition: Psychiatric Adults Patients Date: 2016-07-11 Interventions:
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Recruiting |
Study Name: Study of VTS-270 (2-hydroxypropyl-β-cyclodextrin) to Treat Niemann-Pick Type C1 (NPC1) Disease Condition: Niemann-Pick Disease, Type C Date: 2015-08-18 Interventions:
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